Cover image of Pompe disease guidelines


Life Saving Drugs Program – Pompe disease – Guidelines

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Publication date: 
March 2018
Publication type: 
Intended audience: 
Health sector

These guidelines include:

  • General information about the Life Saving Drugs Program (LSDP)
  • Treatment of Pompe disease through the LSDP
  • Drugs currently available for the treatment of Pompe disease through the LSDP
  • Dosage
  • General, initial and ongoing eligibility requirements
  • LSDP funding conditions
  • Exclusion criteria.