Collections

A collection of resources for health professionals to help people with Gaucher disease (type 1) access the following drugs under the Life Saving Drugs Program: imiglucerase (Cerezyme®), velaglucerase (VPRIV®), taliglucerase (Elelyso®) and eliglustat (Cerdelga®).

A collection of resources for health professionals to help people with infantile-onset lysosomal acid-lipase deficiency disease (LAL-D) access sebelipase alfa (Kanuma®) under the Life Saving Drugs Program.

The PNH review considered the medicine eculizumab. The Expert Panel considered this review at its October 2020 meeting. These resources provide a summary of the review and recommendations.

A collection of resources for health professionals to help people with perinatal- or infantile-onset hypophosphatasia (HPP) access asfotase alfa (Strensiq®) under the Life Saving Drugs Program.

This collection contains the COVID-19 Vaccine Claims Scheme policy, as well as other supporting documents related to the scheme.

A collection of resources for health professionals to help people with mucopolysaccharidosis type I (MPS I) access laronidase (Aldurazyme®) under the Life Saving Drugs Program.

A collection of resources for health professionals to help people with mucopolysaccharidosis type II (MPS II) access idursulfase (Elaprase®) under the Life Saving Drugs Program.

A collection of resources for health professionals to help people with mucopolysaccharidosis type IVA (MPS IVA) access elosulfase alfa (Vimizim®) under the Life Saving Drugs Program.

A collection of resources for health professionals to help people with mucopolysaccharidosis type VI (MPS VI) access galsulfase (Naglazyme®) under the Life Saving Drugs Program (LSDP).

A collection of resources for health professionals to help people with Pompe disease access alglucosidase alfa (Myozyme®) and avalglucosidase alfa (Nexviazyme®) under the Life Saving Drugs Program.

A collection of resources for health professionals to help people with hereditary tyrosinaemia type 1 access nitisinone (Orfadin® and Nityr™) under the Life Saving Drugs Program.

A collection of resources for health professionals to help people with CLN2 disease access cerliponase alfa (Brineura®) under the Life Saving Drugs Program.

A collection of resources for health professionals to help people with Fabry disease access the following drugs under the Life Saving Drugs Program: agalsidase alfa (Replagal®), agalsidase beta (Fabrazyme®).